Original ArticleMonitoring the 3-Year Efficacy of Enzyme Replacement Therapy in Fabry Disease by Repeated Skin Biopsies
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Keywords
α-galactosidase A
angiokeratomas
globotriaosylceramide
lysosomal storage disease
phase 3 trial
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Contributed equally to this study.
Copyright © 2004 The Society for Investigative Dermatology, Inc. All rights reserved.